One awesome way to make an impact this holiday season is to be part of life-changing FA research.
Updates on the gene therapy trials open to people with FA on two continents.
We are excited to fund four new research projects, two targeting the blood problems in Fanconi anemia, and two focusing on understanding cancer in FA.
Clinical and scientific experts met in Pittsburgh to discuss HNSCC in FA and how to improve prevention and treatment outcomes.
Dr. Borgonha will lead FA translational science efforts, including the development of a clinical registry and biobank.
Trials investigating the FDA-approved drug metformin and the natural antioxidant quercetin were funded in early 2018.