An update on three FA clinical trials presented at the 2019 FARF Scientific Symposium
Aldehydes can cause DNA damage to hematopoietic stem cells, leading to bone marrow failure and cancer. Where are we with research into aldehydes in FA? Read this update from the 2019 Symposium.
At the 2019 FARF Scientific Symposium in Chicago, Dr. Grant Rowe became the fourth recipient of the David B. Frohnmayer Early Investigator Award.
Investigators share updates from their current research on the FA pathway and revealed advancements that are reshaping our understanding of the functions of FA genes.
Learn more about Dr. Paula Rio, who works on gene therapy and gene editing in FA
In early October, the U.S. Food and Drug Administration awarded 12 new clinical trial research grants to advance treatments for rare diseases. One of the trials is a phase 2 study of quercetin chemopr