We asked FA families to share with us some of their favorite moments from 2018’s meeting. As memories were shared, we noticed some common themes that families seemed to appreciate most about camp.
Updates on the gene therapy trials open to people with FA on two continents.
We are excited to fund four new research projects, two targeting the blood problems in Fanconi anemia, and two focusing on understanding cancer in FA.
Clinical and scientific experts met in Pittsburgh to discuss HNSCC in FA and how to improve prevention and treatment outcomes.
Dr. Borgonha will lead FA translational science efforts, including the development of a clinical registry and biobank.
FA was once an orphan disease that no one knew anything about, except that it was rare, it affected the blood and it was fatal. Thanks to 30 years of research, this is no longer the case.