Research study is open to participants worldwide to advance understanding and treatments for the rare disease Fanconi anemia.
Learn more about Dr. Paula Rio, who works on gene therapy and gene editing in FA
In early October, the U.S. Food and Drug Administration awarded 12 new clinical trial research grants to advance treatments for rare diseases. One of the trials is a phase 2 study of quercetin chemopr
What is gene therapy in FA, what do we know now, and what's next?
FA organizations in Europe are joining together to form a unified European Group.
With a disease like Fanconi anemia, most of our attention is focused on physical health. Mental health is a component that may get overlooked, yet it is crucial to our overall wellbeing.
Research study is open to participants worldwide to advance understanding and treatments for the rare disease Fanconi anemia.