At the 2019 FARF Scientific Symposium in Chicago, Dr. Grant Rowe became the fourth recipient of the David B. Frohnmayer Early Investigator Award.
Investigators share updates from their current research on the FA pathway and revealed advancements that are reshaping our understanding of the functions of FA genes.
Learn more about Dr. Paula Rio, who works on gene therapy and gene editing in FA
In early October, the U.S. Food and Drug Administration awarded 12 new clinical trial research grants to advance treatments for rare diseases. One of the trials is a phase 2 study of quercetin chemopr
What is gene therapy in FA, what do we know now, and what's next?
FA organizations in Europe are joining together to form a unified European Group.